Nature2 年
ESTABLISHMENT AND CHARACTERIZATION OF ADENOSINE DEAMINASE (ADA)-DEFICIENT T CELL LINES
Congenital deficiency of the purine metabolic enzyme ADA causes severe combined immunodeficiency (SCID). The profound T lymphopenia characteristic of this disease has limited direct investigation ...
precisionmedicineonline2 天
UCLA, University College London Advancing Immune Disorder Gene Therapy Toward FDA Submission
Researchers founded Rarity PBC as a public benefit corporation that will license the IP and develop operations to potentially ...